Paroxysmal Nocturnal Hemoglobinuria: Symptoms, Causes & Treatment
متلازمة PNH
Quick summary
Acquired hereditary defect destroying RBCs. Treated with eculizumab or ravulizumab.
Last updated: 22 July 2026
Medical disclaimer: This content is for educational purposes only and is not a substitute for consulting a qualified physician. Do not use this information for self-diagnosis or self-treatment.
Treatment
- Eculizumab (Soliris).
- Ravulizumab (Ultomiris).
- Pegcetacoplan (Empaveli).
- Iptacopan (Fabhalta).