Spinal Muscular Atrophy: Symptoms, Causes & Treatment
ضمور العضلات الشوكي
Quick summary
Spinal muscular atrophy is a genetic motor neuron disease. Revolutionary therapies: nusinersen, onasemnogene (Zolgensma), risdiplam.
Last updated: 22 July 2026
Medical disclaimer: This content is for educational purposes only and is not a substitute for consulting a qualified physician. Do not use this information for self-diagnosis or self-treatment.
Treatment
- Nusinersen (Spinraza).
- Onasemnogene abeparvovec (Zolgensma).
- Risdiplam (Evrysdi).